Investors + Media

Corporate Profile

AveXis, Inc. is a clinical-stage gene therapy company, dedicated to developing and commercializing novel treatments for patients suffering from rare and life-threatening neurological genetic diseases. Our initial product candidate, AVXS-101, is our proprietary gene therapy currently in development for the treatment of spinal muscular atrophy, or SMA, Type 1, the leading genetic cause of infant mortality, and SMA Type 2. The U.S. Food and Drug Administration, or FDA, has granted AVXS-101 Orphan Drug Designation for the treatment of all types of SMA and Breakthrough Therapy Designation, as well as Fast Track Designation for the treatment of SMA Type 1. In addition to developing AVXS-101 to treat SMA Type 1 and Type 2, we also plan to develop other novel treatments for rare neurological diseases, including Rett syndrome (RTT) and a genetic form of amyotrophic lateral sclerosis (ALS) caused by mutations in the superoxide dismutase 1 (SOD1) gene.

Recent News

More 
04/19/18
AveXis to Present AVXS-101 Data at the Annual Meeting of the American Academy of Neurology
04/09/18
AveXis Enters Agreement to be Acquired by Novartis AG for $8.7 billion
03/27/18
AveXis Gene Therapy Awarded SAKIGAKE Designation for Spinal Muscular Atrophy Type 1

Upcoming Events

More 
There are currently no events scheduled.

E-MAIL ALERTS

Sign up to receive e-mail alerts whenever AveXis, Inc. posts new information to the site. Just enter your e-mail address and click Submit.

IR CONTACT

Jim Goff
Vice President, Investor Relations and Corporate Communications
Phone: (650) 862-4134
E-mail: jgoff@avexis.com


Data provided by Nasdaq. Minimum 15 minutes delayed. View Attributions and Sources

© AveXis, Inc. All Rights Reserved.